By Steven ReinbergHealthDay Reporter
THURSDAY, Oct. 12, 2017 (HealthDay News) -- A U.S. Food and Drug Administration advisory panel on Thursday recommended approval of a gene therapy that could grant the gift of sight to young people with a rare type of inherited vision loss.
The panel members' vote was unanimous. The FDA is not required to follow the advice of its panels, but it usually does.
The treatment, which involves replacing a nonworking gene with a new one, is opening a new world for children and teens with the inherited retinal disease called Leber congenital amaurosis.
"This is a gene therapy that can restore some vision to people who have very limited vision or no vision due to the mutation in the RPE65 gene, and as such, it's a great breakthrough," said Stephen Rose, chief research officer at the Foundation Fighting Blindness.
For those who have already received the therapy, the treatment has been life-changing.
Eleven-year-old Cole Carper got the treatment when he was 8, according to the ...